sofidexFor patientsAre you a clinician? Clinical site

Warning-sign checks

Batten disease: when to get help

Go through these in order and stop at the first one that applies. If you are reading this for someone else, answer for them.

  1. 1

    Is any of this happening now?

    Call 911

    Seek emergency help for:

    • A seizure lasting 5 minutes or longer, unless the person’s emergency plan gives different instructions
    • Repeated seizures without recovery between them
    • Severe trouble breathing, blue or gray lips, or choking that does not clear
    • Unresponsiveness, a serious fall, or a significant head injury
    • A sudden severe reaction during or after an infusion
    Other emergency signs, for anyone
    • Someone who is struggling to breathe, gasping, choking, or cannot get words out
    • Someone who has chest pain, tightness or pressure lasting more than a few minutes
    • Someone who has sudden weakness or drooping on one side of the face or body, slurred speech, or sudden confusion
    • Someone who is unconscious, or cannot be woken
    • Someone who is bleeding heavily and it will not stop with firm pressure
    • Someone who has had a seizure that will not stop, or does not wake up afterwards
    • Someone who has lips or skin that look pale, blue, grey or blotchy
    • Someone who you believe has taken an overdose or swallowed something poisonous
  2. 2

    Is any of this happening?

    Be seen today

    Contact the care team promptly for a meaningful change in seizure pattern, repeated choking, reduced drinking, new breathing symptoms, unexplained decline, or signs of pain.

    Fever, scalp redness, swelling, drainage, or fluid leakage near an implanted reservoir requires urgent medical advice.

  3. 3

    Does any of this apply?

    Book an appointment

    Regular follow-up is usually coordinated by a neurologist or metabolic specialist.

    Depending on the person’s needs, the team may include genetics specialists, eye doctors, rehabilitation therapists, dietitians, speech-language pathologists, pulmonologists, palliative care clinicians, educators, and social workers.

    Routine visits may review seizures, vision, movement, communication, swallowing, nutrition, sleep, breathing, comfort, and caregiver needs.

    Medication effects and equipment fit should also be reassessed.

    People receiving cerliponase alfa need additional monitoring of the implanted delivery system and treatment-related reactions.

The article also says

During a convulsive seizure, protect the person from nearby hazards, place them on their side when possible, and time the seizure.

Do not restrain them or put anything in their mouth.

Families may benefit from genetic counseling after diagnosis and again when considering future pregnancies or testing adult relatives.

Caregivers should also ask about mental health support, respite services, and patient organizations familiar with NCL disorders.

Every sign above is quoted from the sofidex article on Batten disease. If you are not sure, err upward — it is always reasonable to be checked.